Comment from PANTHERx Rare Pharmacy

Summary: Dr. Richard Faris of PANTHERx Rare proposes a specific workshop topic for the RISE Fall Series focused on the role of specialty pharmacies in generating real-world evidence (RWE) for rare diseases. He argues that specialty pharmacies are uniquely positioned to provide longitudinal data on treatment effects, safety, and patient outcomes that can supplement clinical trials and support regulatory decision-making.